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Clinical Characteristics of Cryopyrin-Associated Periodic Syndrome and Long-Term Real-World Efficacy and Tolerability of Canakinumab in Japan: Results of a Nationwide Survey
Arthritis & Rheumatology ( IF 13.3 ) Pub Date : 2024-01-25 , DOI: 10.1002/art.42808
Takayuki Miyamoto 1 , Kazushi Izawa 1 , Sho Masui 2 , Atsue Yamazaki 3 , Yuichi Yamasaki 4 , Tadashi Matsubayashi 5 , Mayuka Shiraki 6 , Hidenori Ohnishi 6 , Junko Yasumura 7 , Kawabe Tomohiro 8 , Takako Miyamae 8 , Tomoyo Matsubara 9 , Naoya Arakawa 10 , Takashi Ishige 10 , Takumi Takizawa 10 , Asami Shimbo 11 , Masaki Shimizu 11 , Naoki Kimura 12 , Yuichi Maeda 13 , Yuta Maruyama 14 , Tomonari Shigemura 14 , Junichi Furuta 15 , Satoshi Sato 16 , Hiroshi Tanaka 17 , Miharu Izumikawa 18 , Masahiro Yamamura 19 , Toshio Hasegawa 20 , Hiroshi Kaneko 21 , Yasuo Nakagishi 22 , Naoko Nakano 23 , Yasunori Iida 24 , Tamaki Nakamura 24 , Hiroyuki Wakiguchi 24 , Takayuki Hoshina 25 , Toshinao Kawai 26 , Kosaku Murakami 27 , Shuji Akizuki 28 , Akio Morinobu 28 , Koichiro Ohmura 29 , Katsuhide Eguchi 30 , Motoshi Sonoda 30 , Masataka Ishimura 30 , Kenji Furuno 31 , Momoko Kashiwado 32 , Masaaki Mori 12, 32 , Kimito Kawahata 32 , Koremasa Hayama 33 , Kumiko Shimoyama 34 , Natsuko Sasaki 35 , Taisuke Ito 36 , Hiroaki Umebayashi 37 , Tae Omori 38 , Seiko Nakamichi 39 , Tomotsune Dohmoto 40 , Yasuyuki Hasegawa 41 , Hisashi Kawashima 42 , Shojiro Watanabe 43 , Yuichiro Taguchi 44 , Haruna Nakaseko 45 , Naomi Iwata 45 , Hiroki Kohno 46 , Taiki Ando 47 , Yasuhiko Ito 48 , Yuko Kataoka 49 , Takako Saeki 50 , Utako Kaneko 51 , Ayako Murase 52 , Seira Hattori 52 , Tomo Nozawa 52 , Kenichi Nishimura 52 , Reiji Nakano 53 , Misa Watanabe 54 , Masato Yashiro 55 , Tomonori Nakamura 56 , Toshihiko Komai 57 , Kentaro Kato 1 , Yoshitaka Honda 1, 58, 59 , Eitaro Hiejima 1 , Atsushi Yonezawa 2 , Kazuhisa Bessho 3 , Satoshi Okada 7 , Osamu Ohara 60 , Junko Takita 1 , Takahiro Yasumi 1 , Ryuta Nishikomori 61 ,
Affiliation  

We assess the clinical characteristics of patients with cryopyrin-associated periodic syndrome (CAPS) in Japan and evaluate the real-world efficacy and safety of interleukin-1 (IL-1) inhibitors, primarily canakinumab.

中文翻译:


日本隐吡啉相关周期性综合征的临床特征以及卡那奴单抗的长期实际疗效和耐受性:全国调查结果



我们评估了日本冷吡蛋白相关周期性综合征 (CAPS) 患者的临床特征,并评估了白细胞介素 1 (IL-1) 抑制剂(主要是卡那单抗)在现实世界中的疗效和安全性。
更新日期:2024-01-25
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